Top
Best
New

Posted by manveerc 2 days ago

Gene-edited pancreatic cells transplanted into a patient with type 1 diabetes(www.wired.com)
239 points | 63 comments
DarwinsToffees 2 days ago|
This is very encouraging, but will take a long time to get to any type of usable treatment because these cells are literally made to evade the immune system they run a whole bunch of other risks. Also cell therapies right now are one of the weakest markets in Biotechs due to the level of costs to develop. This is slightly different since it's Allogenic, but the market seems not very invested in cell therapy.
umvi 2 days ago||
This is great news. Any type of pancreatic function restoration is also potentially good for Type 1.5 (which constitute a sizable chunk of misdiagnosed T2Ds) where the body attacks more slowly (over the course of years) instead of acutely like traditional T1D and so doctors assume it's insulin resistance instead of pancreatic function decline since they both present with the same symptom - hyperglycemia.
tracker1 2 days ago||
It would be nice if fasting insulin and other markers were tested more regularly beyond fasted glucose and a1c, since those can vary for other reasons. Not to mention catching those developing insulin resistance potentially years ahead.
thecosas 1 day ago||
There are also loads of tests for antibodies now; some are even (gasp) free for qualifying people. More here: https://www.breakthrought1d.org/early-detection/#screening-o...
Lu2025 2 days ago||
BTW Covid harms pancreatic cells that produce insulin via autoimmune mechanisms.
rcgy 1 day ago||
That's really exciting news. There's a couple non-immunosuppressed solutions being tested, hopefully one pans out.
thecosas 1 day ago|
Yep, I think vertex is one of the companies trying to tackle an encapsulated set of insulin producing cells.

Neat stuff!

Pwntastic 2 days ago||
https://archive.is/tBrzc
mlhpdx 2 days ago||
This seems like it’s on the right track. Finally something that doesn’t require immunosuppressants.
beached_whale 2 days ago|
It was in people and not mice too. So many of these headlines are in cell cultures or mice.
JackeJR 1 day ago||
N=1 study should not have made it into headlines.

> Although the research marks a milestone in the search for treatments of type 1 diabetes, it’s important to note that the study involved one one participant, who received a low dose of cells for a short period—not enough for the patient to no longer need to control their blood sugar with injected insulin. An editorial by the journal Nature also says that some independent research groups have failed in their efforts to confirm that Sana’s method provides edited cells with the ability to evade the immune system.

thecosas 1 day ago|
Despite that, glad to see it in a human subject.

I’ve had T1D for more than 30 years and have seen every headline under the sun with a “cure” always sometime in the next 5 years, so my expectations are properly tempered.

Still excited by it but a long way from clinics handing this out as a solution (if it’s viable).

consp 1 day ago|||
5 years is modern for a long time. Used to be in the next decades. I've had it for about the same time and about 10 years ago I stopped following all research since it never goes anywhere. I'll wait till they start doing late stage trails to be even interested to read the full report.
JackeJR 1 day ago|||
The thing is that with such a sample, we don't really know

1. If the effect is real. i.e. had the patient not been given the injection, would his/her condition improve spontaneously.

2. Assuming the effect is real, what are the circumstances that make the treatment work for this person.

Not to be overly dismissive of the good work but it is too early to be optimistic about this given the above and the fact that the results were not replicated out of Sana suggest that there is a lot that we need to work out before this becomes a viable treatment for the masses.

The harms of hyping this up is that readers will get their hopes up and then be disappointed when things don't pan out as do most scientific endeavours. Overtime, readers will learn to distrust anything that is being reported because 90% of which do not translate to real world impact. It is hard to get the nuance that "science takes many many failures and iterations" to the public and the more likely outcome of such reporting is general distrust of science when things don't go the way that is hoped for.

gwerbret 1 day ago||
This study's pretty wild -- but this approach has a major downside that they only mentioned in passing in the actual report in the New England Journal of Medicine (paywalled, unfortunately).

To gene-edit these cells, they had to use a lentivirus vector -- a (limited form of a) class of viruses that notably includes HIV. These viral vectors work by splicing themselves into random places in the host cell's DNA. Which is fine, except that there's a non-zero chance that in the process, the virus will initiate a cancer.

When you combine that with a cell deliberately engineered to hide from the immune system, you have the ticket to a very bad time.

Spacecosmonaut 1 day ago|
One would probably engineer these cells with a killswitch, such as doxycycline induced Caspase9 https://pmc.ncbi.nlm.nih.gov/articles/PMC1895037/.

The transgene engineering is totally possible without a viral vector. We engineer cells all the time with recombinase based editing methods for targeted safe harbor insertion of transgenes https://www.nature.com/articles/s41551-024-01227-1. This stuff just permeates through the community slowly.

RHSeeger 2 days ago|
Because it has been commented over and over "oh, type 2 is because you are overweight"...

> We tend to think of type 2 diabetes as a disease that afflicts people who are overweight. But it can also appear in people with perfectly healthy weights—and be more deadly in them. A study published today in the Journal of the American Medical Association indicates that normal-weight people diagnosed with type 2 diabetes have double the risk of dying from heart disease and other causes than overweight people with diabetes.

- https://www.health.harvard.edu/blog/diabetes-can-strike-hard...

(Yes, I know this post is about Type 1... but _all_ of the talk in it when I posted this was about Type 2; and basically blaming the people with it for their condition)

chips_not_fries 2 days ago|||
type 2 is more closely associated with genetics than type 1

https://diabetes.org/about-diabetes/genetics-diabetes

spinach 2 days ago|||
But being overweight is a huge risk factor for developing it and absolutely can contribute to it. I don't how it being more deadly in skinny people detracts from that or is relevant at all.
RHSeeger 2 days ago|||
Because people (who don't know what they're talking about) respond with statements like "you can cure Diabetes Type 2 with diet and exercise", and

- That's false. For _most_ people, you can prevent the symptoms of it with those, but not all. Nor does it _cure_ it, it prevents it from presenting symptoms. The same way that avoiding a food you are allergic to doesn't cure the allergy, it just prevents it from impacting you

- It's insulting to a lot of people that _are_ eating and exercising well, but still battling with Diabetes Type 2

It's wrong and it's insulting.

tracker1 2 days ago||||
Even if you are overweight... it's NOT easy to lose weight.. especially if you've lost a significant amount of weight in your life. You may well have a really dysfunctional metabolism, and most advice is just bad for this case. Many people actually have to eat more of a reduced menu in order to lose weight.

I'm a pretty big fan of carnivore for this, which has its own detractors, and countering half a century of misinformation of meat and fat isn't the easiest thing in the world. And even then, you may still need some level of supplemental insulin for a long while.

That isn't to say I support general gluttony and laziness... but it isn't that easy, and its even harder when people just assume you aren't even trying or have negativity towards you in general. You try to work out and you get dirty looks and stares... you are eating out (healthy options) but again, dirty looks and stares... it doesn't help.

chips_not_fries 2 days ago|||
it's one factor but weight and diet isn't the only component
More comments...